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Browsing by Author Alfano, LN
Showing results 1 to 2 of 2
| Issue Date | Title | Author(s) |
|---|---|---|
| 7-Jun-2022 | INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy | Dowling, JJ; Müller-Felber, W; Smith, BK; Bönnemann, CG; Kuntz, NL; Muntoni, F; Servais, L; Alfano, LN; Beggs, AH; Bilder, DA; Blaschek, A; Duong, T; Graham, RJ; Jain, M; Lawlor, MW; Lee, J; Coats, J; Lilien, C; Lowes, LP; MacBean, V; Neuhaus, S; Noursalehi, M; Pitts, T; Finlay, C; Christensen, S; Rafferty, G; Seferian, AM; Tsuchiya, E; James, ES; Miller, W; Sepulveda, B; Vila, MC; Prasad, S; Rico, S; Shieh, PB |
| 15-Nov-2023 | Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial | Shieh, PB; Kuntz, NL; Dowling, JJ; Müller-Felber, W; Bönnemann, CG; Seferian, AM; Servais, L; Smith, BK; Muntoni, F; Blaschek, A; Foley, AR; Saade, DN; Neuhaus, S; Alfano, LN; Beggs, AH; Buj-Bello, A; Childers, MK; Duong, T; Graham, RJ; Jain, M; Coats, J; MacBean, V; James, ES; Lee, J; Mavilio, F; Miller, W; Varfaj, F; Murtagh, M; Han, C; Noursalehi, M; Lawlor, MW; Prasad, S; Rico, S |